WORLDSymposium™ 2019 Platform and Poster Notifications Sent

Platform and poster notifications were sent to all first authors on Monday, November 5, 2018. The deadline to respond to these notifications is November 12, 2018. Anyone who has not responded by November 12, 2018 deadline will lose this opportunity. Individuals who submitted an abstract for consideration at WORLDSymposium 2019 before the October 1, 2018 submission deadline should check their email. If you or a colleague submitted an abstract as the first author but did not receive a notification, please contact

WORLDSymposium 2019 Late-Breaking Abstract Submission Now Open

Late-breaking abstract submissions for WORLDSymposium 2019 are now open.

WORLDSymposium will be accepting late-breaking abstracts from November 1 to December 1, 2018 for poster presentation only. Click here for more information and to submit a late-breaking abstract.

WORLDSymposium Announces Mark Dant As Recipient of the 2019 Patient Advocate Leader (PAL) Award

Mark Dant, EveryLife Foundation for Rare Diseases Each year, WORLDSymposium recognizes one individual for patient advocacy leadership in the field of lysosomal disease. The 2019 Patient Advocate Leader (PAL) award will be presented to Mark Dant, the current Chairman of the Board of the Washington DC-based EveryLife Foundation for Rare Diseases, a science-based advocacy organization dedicated to accelerating biotech innovations for rare disease treatments through science-driven public policy. Click here to read more.

WORLDSymposium will honor Mark with the 2019 Patient Advocate Leader Award on Wednesday, February 6, 2018 at 7:30 AM prior to the start of the Translational Research presentations at WORLDSymposium 2019.

Click here for more information about the Patient Advocate Leader award.

WORLDSymposium Announces Danilo A. Tagle, PhD, MS as Recipient of 2019 Roscoe O. Brady Award for Innovation and Accomplishment

Danilo A. Tagle, PhD, MS - 2019 WORLDSymposium Roscoe O. Brady Award for Innovation and Accomplishment Recipient Danilo A. Tagle, PhD, MS, is associate director for special initiatives at NCATS. He also recently served as acting director of the NCATS Office of Grants Management and Scientific Review and currently serves as executive secretary to the NCATS Advisory Council and Cures Acceleration Network Review Board. Prior to NCATS, Tagle was a program director for neurogenetics at the National Institute of Neurological Disorders and Stroke (NINDS), where he was involved in developing programs concerning genomics-based approaches for basic and translational research in inherited brain disorders.  Click here to read more.

Dr. Tagle will receive the 2018 award at the opening session of WORLDSymposium 2019 on Tuesday, February 5, 2018 at 7:30 AM.

Click here for more information about the Innovation and Accomplishment award.

WORLDSymposium 2019 Registration Now Open

Plan to attend the 15th Annual WORLDSymposium February 4 – 8, 2019 in Orlando, Florida!

This symposium is designed for basic, translational and clinical researchers, patient advocacy groups, clinicians, and all others who are interested in learning more about the latest discoveries related to lysosomal diseases and the clinical investigation of these advances.

Click here to register.

Deadline to Submit Full-Length Articles to Elsevier was September 1, 2018

The submission deadline for the “Lysosomes” issue of Molecular Genetics and Metabolism was September 1st, 2018. Go to for more information including the Guide for Authors or to Submit Your Paper.

WORLDSymposium 2019 Award Nominations Now Closed

Nominations for the Roscoe O. Brady Award for Innovation and Accomplishment and the Patient Advocate Leader Award closed August 15, 2018. Awards will be presented at WORLDSymposium 2019. Sign up for WORLDSymposium updates to be notified when the award recipients are announced. 

Monday, February 4, 2019: Opening Reception and Awards Ceremony

This year, Monday evening will include the presentation of WORLDSymposium Young Investigator and New Treatment Awards. Plan to arrive early for this special event.

Preliminary Schedule at A Glance

Day Monday
Feb. 4, 2019
Feb. 5, 2019
Feb. 6, 2019
Feb. 7, 2019
Feb. 8, 2019
6:15-7:15 AM Satellite Symposium Satellite Symposium Satellite Symposium
Morning Council of Patient Advocates (COPA) (9:00 AM-12:00 PM) Basic Science: Disease Mechanisms, Pathology, and Biomarkers of Lysosomal Diseases Gene Therapy, Newborn Screening Clinical Trials for Registration1 Council of Research Experts (CORE) (8:00 AM-12:00 PM)
Lunch Satellite Symposium Satellite Symposium Satellite Symposium
Afternoon Emerging Trends 2019 (1:00-5:00 PM) Basic Science: Developing Therapeutic Approaches for Lysosomal Diseases in the Laboratory Translational Research: Clinical Trial Readiness – Preclinical Trial Methods and Studies for Lysosomal Diseases Clinical Trials: Improving Outcomes Post-Registration2
4:30-6:30 PM Poster Session Poster Session Networking Reception (4:30-5:30 PM)
5:15-6:30 PM Award Ceremony & Opening Reception
6:30-8:30 PM Satellite Symposium Satellite Symposium Satellite Symposium
1 Abstracts in the Clinical Trials for Registration category must have an FDA Investigational New Drug (IND) application (Phase I-III clinical trial), an EMA Investigational Medicinal Product Dossier (IMPD), or equivalent.
2 The Clinical Outcomes category includes licensed therapies (Phase IV) and non-interventional studies.

We’re Organizing Research on Lysosomal Diseases

Dates to Remember

July 1, 2018
Abstract submission website open.

August 1, 2018
Online registration and hotel reservations open. Exhibitor prospectus available by request.

September 1, 2018
Deadline for submission of full-length manuscripts for peer-review in the “Lysosomes” issue of Molecular Genetics & Metabolism, February, 2019. Click here to access the Guide for Authors or to Submit Your Paper.

October 1, 2018
Deadline for abstract submission to WORLDSymposium 2019.

November 1 – December 1,  2018
Late breaking abstract submission open.

November 5, 2018
Notification of abstract acceptance for poster or platform presentation at WORLDSymposium 2019.

About WORLDSymposium

The goal of WORLDSymposium is to provide an interdisciplinary forum to explore and discuss specific areas of interest, research and clinical applicability related to lysosomal diseases. Each year, WORLDSymposium hosts a scientific meeting presenting the latest information from basic science, translational research, and clinical trials for lysosomal diseases. This symposium is designed to help researchers and clinicians to better manage and understand diagnostic options for patients with lysosomal diseases, identify areas requiring additional basic and clinical research, public policy and regulatory attention, and identify the latest findings in the natural history of lysosomal diseases.

The Editor

Chester B. Whitley, PhD, MDChester B. Whitley, PhD, MD
WORLDSymposia Editor