Chester B. Whitley, PhD, MDWORLDSymposium is pleased to announce Chester B. Whitley, PhD, MD, will present the Keynote Address The ‘New’ Lysosomal Disease Network on Thursday, February 7, 2019 at 7:30 AM.

Dr. Whitley is Professor of Pediatrics and a Faculty Member of both the Division of Genetics and Metabolism, and the Department of Experimental and Clinical Pharmacology at the University of Minnesota Medical School in Minneapolis, Minnesota. He is certified by the American Board of Medical Genetics and Genomics in the areas of Clinical Biochemical Genetics and Clinical Genetics.

Click here for more information about the Keynote Speaker.


Congratulations to the ten individuals selected to receive the WORLDSymposium Young Investigator Award for 2019. The award is a partial scholarship towards attendance at WORLDSymposium 2019. WORLDSymposium would like to congratulate all of the applicants for their hard work. Award recipients will be recognized at the Award Ceremony and Opening Reception on Monday, February 4 at 5:15 PM in the Regency Foyer.

Click here for the full announcement.

WORLDSymposium 2019 Late-Breaking Abstract Submission Now Closed

Late-breaking abstract submissions for WORLDSymposium 2019 are now closed.

WORLDSymposium accepted late-breaking abstracts from November 1 to December 1, 2018 for poster presentation only. Click here for more information.


The Preliminary Program for WORLDSymposium 2019 is now available. Three full days of new discoveries, cutting-edge research, and updates from ongoing studies will be presented by scientists and clinicians from around the globe.

Monday, February 4, 2019: Opening Reception and Award Ceremony

Plan to arrive early for the Monday evening presentation of WORLDSymposium Young Investigator Award at 5:15 PM, followed by the Opening Reception in the Exhibit Hall at 5:30 PM.

WORLDSymposium Announces Mark Dant As Recipient of the 2019 Patient Advocate Leader (PAL) Award

Mark Dant, EveryLife Foundation for Rare DiseasesEach year, WORLDSymposium recognizes one individual for patient advocacy leadership in the field of lysosomal disease. The 2019 Patient Advocate Leader (PAL) award will be presented to Mark Dant, the current Chairman of the Board of the Washington DC-based EveryLife Foundation for Rare Diseases, a science-based advocacy organization dedicated to accelerating biotech innovations for rare disease treatments through science-driven public policy. Click here to read more.

WORLDSymposium will honor Mark with the 2019 Patient Advocate Leader Award on Wednesday, February 6, 2018 at 7:30 AM prior to the start of the Translational Research presentations at WORLDSymposium 2019.

Click here for more information about the Patient Advocate Leader award.

WORLDSymposium Announces Danilo A. Tagle, PhD, MS as Recipient of 2019 Roscoe O. Brady Award for Innovation and Accomplishment

Danilo A. Tagle, PhD, MS - 2019 WORLDSymposium Roscoe O. Brady Award for Innovation and Accomplishment RecipientDanilo A. Tagle, PhD, MS, is associate director for special initiatives at NCATS. He also recently served as acting director of the NCATS Office of Grants Management and Scientific Review and currently serves as executive secretary to the NCATS Advisory Council and Cures Acceleration Network Review Board. Prior to NCATS, Tagle was a program director for neurogenetics at the National Institute of Neurological Disorders and Stroke (NINDS), where he was involved in developing programs concerning genomics-based approaches for basic and translational research in inherited brain disorders.  Click here to read more.

Dr. Tagle will receive the 2019 Roscoe O. Brady Award for Innovation and Accomplishment at the opening session of WORLDSymposium 2019 on Tuesday, February 5, 2018 at 7:30 AM.

Click here for more information about the Innovation and Accomplishment award.

WORLDSymposium 2019 Registration Open

Plan to attend the 15th Annual WORLDSymposium February 4 – 8, 2019 in Orlando, Florida!

This symposium is designed for basic, translational and clinical researchers, patient advocacy groups, clinicians, and all others who are interested in learning more about the latest discoveries related to lysosomal diseases and the clinical investigation of these advances.

Click here to register.

Preliminary Schedule at A Glance

Day Monday
Feb. 4, 2019
Feb. 5, 2019
Feb. 6, 2019
Feb. 7, 2019
Feb. 8, 2019
6:15-7:15 AM Satellite Symposium Satellite Symposium Satellite Symposium
Morning WORLDFair Council of Patient Advocates (COPA) (9:00 AM-12:00 PM) Basic Science: Disease Mechanisms, Pathology, and Biomarkers of Lysosomal Diseases Gene Therapy, Newborn Screening Clinical Trials for Registration1 Unofficial Events and Ancillary Meetings
Lunch Satellite Symposium Satellite Symposium Satellite Symposium
Afternoon Emerging Trends 2019 (1:00-5:00 PM) Basic Science: Developing Therapeutic Approaches for Lysosomal Diseases in the Laboratory Translational Research: Clinical Trial Readiness – Preclinical Trial Methods and Studies for Lysosomal Diseases Clinical Trials: Improving Outcomes Post-Registration2
4:30-6:30 PM Poster Session Poster Session Networking Reception (4:30-5:30 PM)
5:15-6:30 PM Award Ceremony & Opening Reception Council of Research Experts (CORE) (5:30-7:30 PM)
6:30-8:30 PM Satellite Symposium Satellite Symposium Satellite Symposium
1 Abstracts in the Clinical Trials for Registration category must have an FDA Investigational New Drug (IND) application (Phase I-III clinical trial), an EMA Investigational Medicinal Product Dossier (IMPD), or equivalent.
2 The Clinical Outcomes category includes licensed therapies (Phase IV) and non-interventional studies.

We’re Organizing Research on Lysosomal Diseases

Dates to Remember

July 1, 2018
Abstract submission website open.

August 1, 2018
Online registration and hotel reservations open. Exhibitor prospectus available by request.

September 1, 2018
Deadline for submission of full-length manuscripts for peer-review in the “Lysosomes” issue of Molecular Genetics & Metabolism, February, 2019. Click here to access the Guide for Authors or to Submit Your Paper.

October 1, 2018
Deadline for abstract submission to WORLDSymposium 2019.

November 1 – December 1,  2018
Late breaking abstract submission open.

November 5, 2018
Notification of abstract acceptance for poster or platform presentation at WORLDSymposium 2019.

About WORLDSymposium

The goal of WORLDSymposium is to provide an interdisciplinary forum to explore and discuss specific areas of interest, research and clinical applicability related to lysosomal diseases. Each year, WORLDSymposium hosts a scientific meeting presenting the latest information from basic science, translational research, and clinical trials for lysosomal diseases. This symposium is designed to help researchers and clinicians to better manage and understand diagnostic options for patients with lysosomal diseases, identify areas requiring additional basic and clinical research, public policy and regulatory attention, and identify the latest findings in the natural history of lysosomal diseases.

The Editor

Chester B. Whitley, PhD, MDChester B. Whitley, PhD, MD
WORLDSymposia Editor